Global ETD Search
Search theses and dissertations gathered from participating repositories worldwide. Every result links back to the library that holds it. No account is needed.
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Showing 1 to 1 of 1 for “"orts to develop durable"”.
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Advancing the Development of a CRISPR/Cas9-Based Gene Editing Therapy for Epidermolysis Bullosa
… precisely repairing EB mutations and providing a durable therapy, but this is currently limited by suboptimal editing efficacy. Our research aimed to advance the development of an ex vivo CRISPR-based gene editing therapy by addressing key hurdles hindering clinical translation. To overcome the …