Global ETD Search
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Showing 1 to 2 of 2 for “"Lumacaftor-Ivacaftor"”.
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Burden of Illness and Pharmacoeconomic Evaluation of Lumacaftor/Ivacaftor in Cystic Fibrosis
… (2) to conduct a pharmacoeconomic evaluation of lumacaftor/ivacaftor in the treatment of CF. <strong></strong></p> <p><strong>Methods:</strong> The study was conducted in two parts. Part 1 involved a retrospective analysis using individuals in MEPS database with an International Classification of …
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Real-world Orkambi Cork (ROCK) study - a prospective 12 months analysis addressing the impact of CFTR modulation in patients with cystic fibrosis homozygous for F508del CFTR variant
… of CFTR dysfunction. The introduction of Lumacaftor-Ivacaftor marks a pivotal shift, allowing researchers to assess the impact of CFTR function restoration on both pulmonary disease and extrapulmonary manifestations. Globally, approximately 82% of individuals with CF are homozygous for the …